In people with Duchenne muscular dystrophy
, their stem cells do not produce enough of the cells that will become muscle cells.
Patients with muscular dystrophy
usually require orthopedic surgeries early in life, scoliosis correction, muscle biopsies, tendon release, or tendon transfers.
The company hopes to meet with the FDA to discuss the CAP-1002 development program for treatment of Duchenne muscular dystrophy
, and specifically the HOPE-2 Trial.
The company's lead candidate, CAP-1002, is an "off-the-shelf" cardiac cell therapy that is currently in clinical development for the treatment of Duchenne muscular dystrophy
A total of 100 patients belonging to all age groups, both male and female with strong clinical suspicion of muscular dystrophy
, irrespective of positive family history, were included by convenient sampling technique.
* The report assesses Muscular Dystrophy
therapeutics based on drug target, mechanism of action (MoA), route of administration (RoA) and molecule type
The student nurse said: "It's great that millions of pounds have been given to help improve treatment for those with Duchenne muscular dystrophy
Since Jack's diagnosis, the Gauder family have raised over PS50,000 for Muscular Dystrophy
UK, through their Family Fund, Fighting Back for Jack.
* The report reviews key players involved in the therapeutics development for Becker Muscular Dystrophy
and enlists all their major and minor projects
The Ryan's Quest Foundation was founded by Hamilton, New Jersey residents David and Maria Schultz on behalf of their son Ryan and thousands of other young men diagnosed with Duchenne muscular dystrophy
, a life limiting disorder for which there is no cure.
Cognitive and adaptive deficits in young children with Duchenne muscular dystrophy
KEY WORDS: Becker muscular dystrophy
, dystrophin gene, exon, deletion